๐ฌ Current Disease Focus:
Task Progress: 0%
๐ฅ Active Problem Solvers
0
๐ Experts collaborating globally
โก Current Task Assignment
๐งฌ Genetic Analysis
๐ Matching experts to specific tasks
๐ Resource Allocation by Research Phase:
๐ Data Analysis
๐งช Experimental Design
๐ฌ Clinical Trials
๐ Treatment Development
This clinical study is in participants with Amyotrophic Lateral Sclerosis a...
Status
Recruiting
Location
Macquarie University Hospital
Start Date
2026-01-12
Trial ID
NCT07401121
Treatments Being Tested
Title: Intrathecal Administration of scAAV9/JeT-GAN for the Treatment of Gi...
Status
Completed
Location
National Institutes of Health Clinical Center
Start Date
2015-04-24
Trial ID
NCT02362438
Treatments Being Tested
RGX-121 is a gene therapy which is intended to deliver a functional copy of...
Status
Active Not Recruiting
Location
St. Peter's University Hospital
Start Date
2025-11-25
Trial ID
NCT07236606
Treatments Being Tested
The purpose of this trial is to evaluate safety and efficacy of intrathecal...
Status
Enrolling By Invitation
Location
Shanghai Children's Medical Center Affiliated to Shanghai Jiao Tong University School of Medicine
Start Date
2025-03-10
Trial ID
NCT06888661
Treatments Being Tested
This is a controlled, open-label, single-ascending dose study to evaluate t...
Status
Active Not Recruiting
Location
David Geffen School of Medicine at UCLA
Start Date
2017-12-06
Trial ID
NCT03368742
Treatments Being Tested
The purpose of this trial is to evaluate the safety and tolerability of int...
Status
Terminated
Location
UCLA
Start Date
2017-12-14
Trial ID
NCT03381729
Treatments Being Tested
The study will evaluate the tolerability, safety and efficacy of gene thera...
Status
Recruiting
Location
Republican Scientific and Practical Center Mother and Child
Start Date
2025-09-30
Trial ID
NCT07673809
Treatments Being Tested
This is a phase 1/2, open-label, single dose study to evaluate the safety a...
Status
Completed
Location
Nationwide Children's Hosptial
Start Date
2016-05
Trial ID
NCT02725580
Treatments Being Tested
GM2 gangliosidoses are a group of autosomal recessive neurodegenerative dis...
Status
Active Not Recruiting
Location
Queen's University/Kingston Health Sciences Centre
Start Date
2021-03-12
Trial ID
NCT04798235
Treatments Being Tested
This trial includes dose-escalating part (phase 1) and dose confirming part...
Status
Active Not Recruiting
Location
Shanghai
Start Date
2024-07-02
Trial ID
NCT06432140
Treatments Being Tested